Senior Director, US Medical Lead, Growth Related Conditions

OVERVIEW: BioMarin US Medical Affairs For more than two decades, going our own way has led to countless breakthroughs, bettering the lives of those suffering from rare genetic diseases. In 1997 we were founded to make a big difference in small patient populations. Now we seek to make an even greater impact by applying the same science-driven, patient-forward approach that propelled our last 25 years of drug development to larger genetic disorders, as well as genetic subsets of more common conditions. Through our unparalleled expertise in genetics and molecular biology, we will continue to develop targeted therapies that address the root cause of the conditions we seek to treat. Applying our knowledge to make a transformative impact is not just a calling, but an obligation to those who will benefit most. The end goal has always been better lives and now we can reach more. And the more people we reach, the more our impact can grow. We transform lives through genetic discovery. Our CultureOur desire to make a positive impact on our patients extends to our employees and BioMarin is committed to fostering an inclusive environment where every person feels seen, valued, and heard – so employees can thrive in all areas of their lives, in and outside of work. We seek to provide an open, flexible, and friendly work environment to empower people and to provide them with the ability to develop their long-term careers. Ultimately, we want to be an organization where people enjoy coming to work and take pride in our efforts to help patients. BioMarin’s Research & Development group is responsible for everything from research and discovery to post-market clinical development. Research & Development involves all bench and clinical research and the associated groups that support those endeavors. Our teams work on developing first-in-class or best-in-class therapeutics that provide meaningful advances to patients. Come join our team and make a meaningful impact on patients’ lives. Global Medical Affairs (GMAF) is a department within BioMarin’s Worldwide R&D organization.  GMAF’s purpose is to drive BioMarin’s scientific strategy to improve access and health outcomes for patients BIOMARIN US MEDICAL AFFAIRSUS Medical Mission: To accelerate the integration of our medicine in standard of care.  Develop and execute patient-centric, insights-driven medical strategies to improve healthcare outcomes and the appropriate use of our medicines through scientific engagement, education, and evidence generation. SUMMARY DESCRIPTIONThis position is embedded in the US Medical Affairs organization and is responsible for medical leadership for BioMarin’s growth-related conditions medicines and programs. This responsibility includes leadership and direction across US medical team to ensure strategic alignment and integration at the global level of regionally driven priorities. This individual will interface externally with healthcare professionals, clinical investigators, regulatory agencies amongst others as well as with cross-functional internal BioMarin teams providing medical insights to drive scientific strategy within integrated brand plans and to inform clinical development and life cycle plans related to this therapeutic area. This individual will be the scientific reference point at the US level, representing the department and the company at key internal and external activities and events in relation to the therapeutic area.                                                                                                                                                                                           KEY RESPONSIBILITIES:  Medical Lead – US Medical

• Lead US medical strategic planning, prioritization, and execution oversight of Growth Conditions medical activities. Assign and align functionally and cross-functionally on objectives, deliverables, roles & responsibilities
• Partnering with cross-functional BioMarin teams (including marketing, market access, clinical development and others) in the development and execution of integrated VOXZOGO brand and launch strategies, robust LCM and pipeline development plans
• Ensuring timely GMAF leadership team awareness and alignment on key program needs and opportunities and ensure representation of GMAF aligned position in internal and external forums and processes
• Providing medical input into development, execution, and interpretation of clinical protocols.  This includes review of draft independent research protocols, reports, and manuscripts; oversight of clinical registries and other post-marketing commitment; support evaluation of safety issues in collaboration with Medical Monitors and other teams; review of study results in study reports
• Develop high-performing US medical Growth related Conditions team of direct reports and matrix partners.
• Direct interaction